From Isolation to Empowerment: How Performing Arts Can Transform the Lives of Those with Rare Diseases
- May 7
- 7 min
Thought Leadership in Mental Health For Rare Diseases
- May 6
- 4 min
Rare Diseases, Mental Health Issues, and What We Can Do About It
- Mar 21
- 6 min
Beyond the Skin and Muscles: Understanding Dermatomyositis
- Feb 19
- 2 min
FDA Extends Priority Review Period for Kresladi/ RP-L 201 in Treating Severe Leukocyte Adhesion Deficiency-I (LAD-1)
- Feb 16
- 7 min
From Struggle to Seeking Solutions: The Reality of Rare Disease Diagnostic Methods
- Feb 2
- 6 min
Navigating the Complexity of Danon Disease
- Jan 29
- 8 min
Beyond the Bloodstream: Understanding Pyruvate Kinase Deficiency (PKD)
- Jan 25
- 6 min
Facing Leukocyte Adhesion Deficiency (LAD): Types, Symptoms, and Progress in Diagnosis and Treatment
- Jan 23
- 4 min
A Discussion with Michael Kornhauser - A Rare Disease Ally in Clinical Research
- Jan 18
- 3 min
Milestone in Gene Therapy: Casgevy Approved for Transfusion-Dependent Beta Thalassemia
- Jan 16
- 7 min
Aplastic Anemia: Unravelling the Mystery of Bone Marrow Failure
- Jan 11
- 13 min
Into the Depths of Multiple Sclerosis: An Exploration from Symptoms to Treatment Options
- Dec 29, 2023
- 7 min
Understanding Ehlers-Danlos Syndrome (EDS)
- Dec 12, 2023
- 3 min
New Horizon in PNH Treatment: FDA Approves First Oral Drug
- Nov 10, 2023
- 4 min
Achondroplasia: Insights into Genetics, Diagnosis, and Treatment Options
- Nov 8, 2023
- 9 min
Understanding Hemophilia: Symptoms, Diagnosis, and Treatment Options
- Nov 6, 2023
- 3 min
New Hope for Pediatric Patients: Bosutinib's Approval in Treating Chronic Phase Ph+ CML
- Nov 3, 2023
- 9 min
10 Top Picks on Amazon to Help Ease Insomnia: Sleep Aid Technology and Gadgets for 2023
- Nov 1, 2023
- 3 min
Assessing Safety and Effectiveness of Damoctocog Alfa Pegol in Hemophilia A Patients