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A Historic Breakthrough in Huntington’s Disease: Gene Therapy Offers New Hope
For decades, Huntington’s disease had no treatment that could alter its course. The new AMT 130 gene therapy trial shows promise in slowing disease progression, marking a historic milestone for patients, families, and the broader rare disease community.
The Rare360 Editorial Team
Sep 26, 20257 min read
The Genetic Puzzle Solved: Why Some People Stay Symptom-Free Despite Disease Genes
Why do some people inherit disease-causing genes but show no symptoms?
The Rare360 Editorial Team
Jan 21, 20253 min read
From CRISPR to Jumping Genes: The Next Breakthrough in Genetic Science
New research on "jumping genes" could lead to safer, more precise gene-editing techniques.
The Rare360 Editorial Team
Oct 3, 20244 min read
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