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A Historic Breakthrough in Huntington’s Disease: Gene Therapy Offers New Hope
For decades, Huntington’s disease had no treatment that could alter its course. The new AMT 130 gene therapy trial shows promise in slowing disease progression, marking a historic milestone for patients, families, and the broader rare disease community.
The Rare360 Editorial Team
Sep 26, 20257 min read
Genetic Blueprints in Mental Health: How Pharmacogenomic Testing is Changing the Game
Pharmacogenomic (PGx) testing is revolutionizing how doctors prescribe mental health medications, especially for rare disease patients.
The Rare360 Editorial Team
Oct 2, 20246 min read
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