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From Isolation to Empowerment: How Performing Arts Can Transform the Lives of Those with Rare Diseases
Discover how performing arts can uplift individuals with rare diseases, addressing mental health challenges and fostering empowerment.
The Rare360 Editorial Team
May 9, 20247 min read
Thought Leadership in Mental Health For Rare Diseases
A discussion with Mental Health for Rare Thought Leader JC Muyl.
The Rare360 Editorial Team
May 7, 20247 min read
Rare Diseases, Mental Health Issues, and What We Can Do About It
For the rare disease community, mental health is not just a topic to discuss during the month of May. Mental health must remain a priority.
The Rare360 Editorial Team
May 6, 20244 min read
Beyond the Skin and Muscles: Understanding Dermatomyositis
Explore the complexities of living with dermatomyositis, a rare autoimmune disorder affecting both muscles and skin.
The Rare360 Editorial Team
Mar 21, 20246 min read
FDA Extends Priority Review Period for Kresladi/ RP-L 201 in Treating Severe Leukocyte Adhesion Deficiency-I (LAD-1)
Explore the FDA's extension of the priority review period for Kresladi, a groundbreaking gene therapy for severe LAD-1
The Rare360 Editorial Team
Feb 19, 20242 min read
From Struggle to Seeking Solutions: The Reality of Rare Disease Diagnostic Methods
From genetic testing to AI, explore the evolving landscape shaping the future of rare disease diagnosis.
The Rare360 Editorial Team
Feb 16, 20247 min read
Navigating the Complexity of Danon Disease
Unveil the complexities of Danon Disease –a rare multisystem disorder. From genetics to management, explore the latest insights in this blog
The Rare360 Editorial Team
Feb 2, 20246 min read
Beyond the Bloodstream: Understanding Pyruvate Kinase Deficiency (PKD)
Discover the genetic intricacies of Pyruvate Kinase Deficiency, its diverse symptoms, diagnostic challenges, & cutting-edge treatment option
The Rare360 Editorial Team
Jan 29, 20248 min read
Facing Leukocyte Adhesion Deficiency (LAD): Types, Symptoms, and Progress in Diagnosis and Treatment
Delve into Leukocyte Adhesion Deficiency (LAD): genetic causes, symptoms, and treatment strategies.
The Rare360 Editorial Team
Jan 25, 20246 min read
A Discussion with Michael Kornhauser - A Rare Disease Ally in Clinical Research
Discussing the impact of clinical studies on patients’ lives and Michael’s perspective as a clinical trials operations specialist.
The Rare360 Editorial Team
Jan 23, 20244 min read
Milestone in Gene Therapy: Casgevy Approved for Transfusion-Dependent Beta Thalassemia
Explore the FDA's groundbreaking approval of CASGEVY™ the treatment of transfusion-dependent beta-thalassemia (TDT).
The Rare360 Editorial Team
Jan 18, 20243 min read
Aplastic Anemia: Unravelling the Mystery of Bone Marrow Failure
Explore Aplastic Anemia's complexities—autoimmune links, diverse causes, evolving treatments.
The Rare360 Editorial Team
Jan 16, 20247 min read
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